gene therapy

Key Findings and Next Steps

Where do we want our hair cell regeneration research to be in three years’ time, and what will it take to get us there?

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Gene Therapy for Hearing Loss: Interpreting Preliminary Clinical Trial Results

Our independent analysis of the clinical trials’ published data yields the following insights on gene therapy for hearing loss from otoferlin variants. The clinical trials provide the first validation of pharmacological treatments for hearing loss.

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Seeing Friends at ARO in Anaheim

Palpable excitement was raised by reports from researchers who have recently published results of landmark gene therapy trials in young children targeting the otoferlin gene.

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Recruiting for a Gene Therapy Trial

Right now we are actively recruiting volunteers with hearing loss to participate in an outpatient research study to understand the genes that cause non-syndromic autosomal dominant hearing loss (DFNA).

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